JP2018509154A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2018509154A5 JP2018509154A5 JP2017547425A JP2017547425A JP2018509154A5 JP 2018509154 A5 JP2018509154 A5 JP 2018509154A5 JP 2017547425 A JP2017547425 A JP 2017547425A JP 2017547425 A JP2017547425 A JP 2017547425A JP 2018509154 A5 JP2018509154 A5 JP 2018509154A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- nucleotide sequence
- mammal
- motomeko
- sequence encoding
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562131661P | 2015-03-11 | 2015-03-11 | |
| US62/131,661 | 2015-03-11 | ||
| PCT/US2016/022072 WO2016145345A1 (en) | 2015-03-11 | 2016-03-11 | Rp2 and rpgr vectors for treating x-linked retinitis pigmentosa |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020167984A Division JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2018509154A JP2018509154A (ja) | 2018-04-05 |
| JP2018509154A5 true JP2018509154A5 (2) | 2019-04-18 |
| JP6935049B2 JP6935049B2 (ja) | 2021-09-15 |
Family
ID=56879752
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2017547425A Active JP6935049B2 (ja) | 2015-03-11 | 2016-03-11 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
| JP2020167984A Pending JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020167984A Pending JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Country Status (6)
| Country | Link |
|---|---|
| US (2) | US10646588B2 (2) |
| EP (2) | EP3719134B1 (2) |
| JP (2) | JP6935049B2 (2) |
| AU (1) | AU2016228751B2 (2) |
| CA (1) | CA2979229A1 (2) |
| WO (1) | WO2016145345A1 (2) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2016228751B2 (en) | 2015-03-11 | 2022-01-13 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Rp2 vectors for treating x-linked retinitis pigmentosa |
| SG11202004527YA (en) | 2017-11-15 | 2020-06-29 | Univ Michigan Regents | Viral vectors comprising rdh12 coding regions and methods of treating retinal dystrophies |
| TW202028225A (zh) * | 2018-09-21 | 2020-08-01 | 英商夜星克有限公司 | 用於治療色素性視網膜炎之組合物及方法 |
| US20220054655A1 (en) * | 2019-02-22 | 2022-02-24 | University Of Massachusetts | Oxr1 gene therapy |
| EP4022065A4 (en) * | 2019-08-30 | 2024-02-14 | Baylor College Of Medicine | GENE EXPRESSION REGULATION SYSTEM |
| US20230142852A1 (en) * | 2020-03-04 | 2023-05-11 | University Of Massachusetts | Compositions and methods for modulating rpgr expression |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| IL128736A0 (en) | 1996-09-06 | 2000-01-31 | Univ Pennsylvania | Methods using cre-lox for production of recombinant adeno-associated viruses |
| DK2242840T3 (da) | 2008-01-29 | 2019-10-21 | Applied Genetic Tech Corporation | Produktion af rekombinant adeno-associeret virus under anvendelse af bhk-celler i suspension |
| US20100081707A1 (en) * | 2008-02-21 | 2010-04-01 | Ali Robin R | Devices and methods for delivering polynucleotides into retinal cells of the macula and fovea |
| AU2012258525B2 (en) | 2011-05-26 | 2017-02-23 | University Of Washington | Cell and gene based methods to improve cardiac function |
| EP2872183B1 (en) * | 2012-07-11 | 2018-09-26 | The Trustees Of The University Of Pennsylvania | Aav-mediated gene therapy for rpgr x-linked retinal degeneration |
| AU2014216160B2 (en) * | 2013-02-15 | 2017-03-30 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | AAV8 retinoschisin expression vector for treating X-linked retinoschisis |
| ES2697249T3 (es) * | 2013-03-11 | 2019-01-22 | Fond Telethon | miR-204 y miR-211 y usos de los mismos |
| CA2945965C (en) | 2014-04-15 | 2022-11-01 | Applied Genetic Technologies Corporation | Codon optimized nucleic acid encoding a retinitis pigmentosa gtpase regulator (rpgr) |
| IL248102B (en) * | 2014-05-02 | 2022-07-01 | Genzyme Corp | aav vectors for gene therapy of the central nervous system and retina |
| GB201412011D0 (en) * | 2014-07-04 | 2014-08-20 | Ucl Business Plc | Treatments |
| PT3191139T (pt) * | 2014-07-24 | 2020-11-05 | Massachusetts Eye & Ear Infirmary | Terapia do gene rpgr para retinite pigmentosa |
| RS63416B1 (sr) * | 2015-03-03 | 2022-08-31 | Fond Telethon | Sistem višestrukih vektora i njegove primene |
| AU2016228751B2 (en) | 2015-03-11 | 2022-01-13 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Rp2 vectors for treating x-linked retinitis pigmentosa |
-
2016
- 2016-03-11 AU AU2016228751A patent/AU2016228751B2/en active Active
- 2016-03-11 EP EP20176667.2A patent/EP3719134B1/en active Active
- 2016-03-11 WO PCT/US2016/022072 patent/WO2016145345A1/en not_active Ceased
- 2016-03-11 EP EP16762623.3A patent/EP3268481B1/en active Active
- 2016-03-11 US US15/556,746 patent/US10646588B2/en active Active
- 2016-03-11 JP JP2017547425A patent/JP6935049B2/ja active Active
- 2016-03-11 CA CA2979229A patent/CA2979229A1/en active Pending
-
2020
- 2020-04-21 US US16/854,605 patent/US11617801B2/en active Active
- 2020-10-02 JP JP2020167984A patent/JP2021019611A/ja active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2018509154A5 (2) | ||
| JP6831779B2 (ja) | 修飾された第ｉｘ因子、並びに、細胞、器官及び組織への遺伝子導入のための組成物、方法及び使用 | |
| JP7374119B2 (ja) | 減少した肝臓向性を有するＡＡＶ９とＡＡＶｒｈ７４とのハイブリッド組換えアデノ随伴ウイルス血清型 | |
| US20220331409A1 (en) | Factor ix gene therapy | |
| JP2020514286A5 (2) | ||
| JP6805174B2 (ja) | 神経成長因子シグナルペプチド及び副甲状腺ホルモンを含むａａｖ分離株及び融合タンパク質 | |
| JP2016538885A5 (2) | ||
| JP2015523379A5 (2) | ||
| JP2019523648A5 (2) | ||
| JP2018537984A5 (2) | ||
| EP4272728A3 (en) | Adeno-associated virus variant capsids and use for inhibiting angiogenesis | |
| JP2019524090A5 (2) | ||
| CA3024449A1 (en) | Compositions and methods of treating huntington's disease | |
| JP2018512125A (ja) | 多重ベクターシステム及びその使用 | |
| JP2019502378A5 (2) | ||
| KR20160033217A (ko) | 변종 ａａｖ 및 조성물, 세포, 기관 및 조직으로의 유전자 전이를 위한 방법 및 용도 | |
| KR20170084012A (ko) | 지혈 장애의 치료를 위한 변이체 인자 viii의 패키징 및 발현을 위한 개선된 발현 카세트 | |
| JP2016500519A5 (2) | ||
| JP2020073536A5 (2) | ||
| JP2021500922A5 (2) | ||
| Hollinger et al. | Viral vector-mediated gene therapies | |
| JP2022529782A (ja) | シュタルガルト病（ａｂｃａ４）の遺伝子治療 | |
| JP2017523239A5 (2) | ||
| JP2021502978A5 (2) | ||
| JP2021510301A5 (2) |