CA3014704C - Thérapie génique pour le traitement de maladies degeneratives de la rétine - Google Patents

Thérapie génique pour le traitement de maladies degeneratives de la rétine

Info

Publication number
CA3014704C
CA3014704C CA3014704A CA3014704A CA3014704C CA 3014704 C CA3014704 C CA 3014704C CA 3014704 A CA3014704 A CA 3014704A CA 3014704 A CA3014704 A CA 3014704A CA 3014704 C CA3014704 C CA 3014704C
Authority
CA
Canada
Prior art keywords
nucleic acid
acid vector
aav
aav nucleic
vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Active
Application number
CA3014704A
Other languages
English (en)
Other versions
CA3014704A1 (fr
Inventor
Stylianos Michalakis
Martin Biel
Mathias Seeliger
Christian Schoen
Original Assignee
Eyeserv GmbH
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Priority claimed from EP16156902.5A external-priority patent/EP3210632B1/fr
Application filed by Eyeserv GmbH filed Critical Eyeserv GmbH
Publication of CA3014704A1 publication Critical patent/CA3014704A1/fr
Application granted granted Critical
Publication of CA3014704C publication Critical patent/CA3014704C/fr
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

Abstract

La présente invention concerne un polynucléotide conçu pour traiter des maladies dégénératives de la rétine telles que la rétinite pigmentaire (RP), un acide nucléique vecteur comprenant ledit polynucléotide, une composition pharmaceutique comprenant ledit acide nucléique vecteur, un kit comprenant ledit polynucléotide ou ledit acide nucléique vecteur, une méthode de fabrication de cet acide nucléique vecteur, et une méthode de traitement de maladies dégénératives de la rétine.
CA3014704A 2016-02-23 2017-02-23 Thérapie génique pour le traitement de maladies degeneratives de la rétine Active CA3014704C (fr)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP16156902.5 2016-02-23
EP16156902.5A EP3210632B1 (fr) 2016-02-23 2016-02-23 Thérapie génique pour le traitement d'une maladie de dégénérescence rétinienne
PCT/EP2017/054230 WO2017144611A1 (fr) 2016-02-23 2017-02-23 Thérapie génique pour le traitement de maladies dégénératives de la rétine

Publications (2)

Publication Number Publication Date
CA3014704A1 CA3014704A1 (fr) 2017-08-31
CA3014704C true CA3014704C (fr) 2026-03-17

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