CL2014003464A1 - Método para mejorar la integridad deteriorada de la unión neuromuscular que comprende la administración de una composición que comprende un vector viral adeno-asociado recombinante (raav) que comprende una molécula de ácido nucleico que codifica la alfa-glucosidasa ácida (gaa). - Google Patents

Método para mejorar la integridad deteriorada de la unión neuromuscular que comprende la administración de una composición que comprende un vector viral adeno-asociado recombinante (raav) que comprende una molécula de ácido nucleico que codifica la alfa-glucosidasa ácida (gaa).

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Publication number
CL2014003464A1
CL2014003464A1 CL2014003464A CL2014003464A CL2014003464A1 CL 2014003464 A1 CL2014003464 A1 CL 2014003464A1 CL 2014003464 A CL2014003464 A CL 2014003464A CL 2014003464 A CL2014003464 A CL 2014003464A CL 2014003464 A1 CL2014003464 A1 CL 2014003464A1
Authority
CL
Chile
Prior art keywords
raav
gaa
glucosidase
administration
improving
Prior art date
Application number
CL2014003464A
Other languages
English (en)
Inventor
Barry John Byrne
Darin J Falk
Christina Pacak
Lara Robert Deruisseau
Cathryn Mah
David D Fuller
Original Assignee
Univ Florida
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Priority claimed from US13/527,350 external-priority patent/US20120322861A1/en
Application filed by Univ Florida filed Critical Univ Florida
Publication of CL2014003464A1 publication Critical patent/CL2014003464A1/es

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    • C12N2750/14152—Methods of production or purification of viral material relating to complementing cells and packaging systems for producing virus or viral particles

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CL2014003464A 2012-06-19 2014-12-19 Método para mejorar la integridad deteriorada de la unión neuromuscular que comprende la administración de una composición que comprende un vector viral adeno-asociado recombinante (raav) que comprende una molécula de ácido nucleico que codifica la alfa-glucosidasa ácida (gaa). CL2014003464A1 (es)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US13/527,350 US20120322861A1 (en) 2007-02-23 2012-06-19 Compositions and Methods for Treating Diseases

Publications (1)

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CL2014003464A1 true CL2014003464A1 (es) 2015-06-12

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CL2014003464A CL2014003464A1 (es) 2012-06-19 2014-12-19 Método para mejorar la integridad deteriorada de la unión neuromuscular que comprende la administración de una composición que comprende un vector viral adeno-asociado recombinante (raav) que comprende una molécula de ácido nucleico que codifica la alfa-glucosidasa ácida (gaa).

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US (2) US10912804B2 (es)
EP (4) EP4124346A3 (es)
JP (1) JP2015523998A (es)
KR (1) KR20150020250A (es)
CN (1) CN104619354A (es)
AU (1) AU2013277215A1 (es)
BR (1) BR112014031788A2 (es)
CA (1) CA2875523A1 (es)
CL (1) CL2014003464A1 (es)
CY (1) CY1123485T1 (es)
DK (1) DK3292875T3 (es)
ES (1) ES2813558T3 (es)
HK (1) HK1209633A1 (es)
HR (1) HRP20201224T1 (es)
HU (1) HUE051632T2 (es)
IL (1) IL236298A0 (es)
LT (1) LT3292875T (es)
MX (1) MX2014015985A (es)
PL (1) PL3292875T3 (es)
PT (1) PT3292875T (es)
RS (1) RS61055B1 (es)
RU (1) RU2015101276A (es)
SI (1) SI3292875T1 (es)
SM (1) SMT202000445T1 (es)
WO (1) WO2013192317A2 (es)

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