EP4780465A2 - Liposomale formulierungen zur behandlung von gm1-mangelzuständen - Google Patents

Liposomale formulierungen zur behandlung von gm1-mangelzuständen

Info

Publication number
EP4780465A2
EP4780465A2 EP24869128.9A EP24869128A EP4780465A2 EP 4780465 A2 EP4780465 A2 EP 4780465A2 EP 24869128 A EP24869128 A EP 24869128A EP 4780465 A2 EP4780465 A2 EP 4780465A2
Authority
EP
European Patent Office
Prior art keywords
ganglioside
sphingosine
composition
gal
acid
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
EP24869128.9A
Other languages
English (en)
French (fr)
Inventor
Shawn Defrees
Current Assignee (The listed assignees may be inaccurate. Google has not performed a legal analysis and makes no representation or warranty as to the accuracy of the list.)
Seneb Biosciences Inc
Original Assignee
Seneb Biosciences Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Seneb Biosciences Inc filed Critical Seneb Biosciences Inc
Publication of EP4780465A2 publication Critical patent/EP4780465A2/de
Pending legal-status Critical Current

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00—Medicinal preparations characterised by special physical form
    • A61K9/10—Dispersions; Emulsions
    • A61K9/127—Synthetic bilayered vehicles, e.g. liposomes or liposomes with cholesterol as the only non-phosphatidyl surfactant
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/70—Carbohydrates; Sugars; Derivatives thereof
    • A61K31/7028—Compounds having saccharide radicals attached to non-saccharide compounds by glycosidic linkages
    • A61K31/7032—Compounds having saccharide radicals attached to non-saccharide compounds by glycosidic linkages attached to a polyol, i.e. compounds having two or more free or esterified hydroxy groups, including the hydroxy group involved in the glycosidic linkage, e.g. monoglucosyldiacylglycerides, lactobionic acid, gangliosides

Landscapes

  • Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Epidemiology (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Molecular Biology (AREA)
  • Dispersion Chemistry (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicinal Preparation (AREA)
  • Saccharide Compounds (AREA)
EP24869128.9A 2023-09-19 2024-09-19 Liposomale formulierungen zur behandlung von gm1-mangelzuständen Pending EP4780465A2 (de)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US202363583816P 2023-09-19 2023-09-19
PCT/US2024/047401 WO2025064617A2 (en) 2023-09-19 2024-09-19 Liposomal formulations for treatment of gm1 deficiencies

Publications (1)

Publication Number Publication Date
EP4780465A2 true EP4780465A2 (de) 2026-07-29

Family

ID=95073594

Family Applications (1)

Application Number Title Priority Date Filing Date
EP24869128.9A Pending EP4780465A2 (de) 2023-09-19 2024-09-19 Liposomale formulierungen zur behandlung von gm1-mangelzuständen

Country Status (2)

Country Link
EP (1) EP4780465A2 (de)
WO (1) WO2025064617A2 (de)

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE69432513T2 (de) * 1993-01-22 2003-12-24 Sloan-Kettering Institute For Cancer Research, New York Gangliosid-klh-konjugatimastoffe mit qs-21
JP2005500058A (ja) * 2001-08-17 2005-01-06 ネオーズ テクノロジーズ， インコーポレイテッド シアリル化したオリゴサッカリドの化学的酵素的合成
US20250289844A1 (en) * 2022-04-29 2025-09-18 Seneb Biosciences, Inc. Treatment of gm1 deficiencies

Also Published As

Publication number Publication date
WO2025064617A2 (en) 2025-03-27
WO2025064617A3 (en) 2025-05-08

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