CL2014002198A1 - Composiciones de vector de virus adenoasociado (aav) y métodos para transferencia de genes a células, órganos y tejidos - Google Patents

Composiciones de vector de virus adenoasociado (aav) y métodos para transferencia de genes a células, órganos y tejidos

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Publication number
CL2014002198A1
CL2014002198A1 CL2014002198A CL2014002198A CL2014002198A1 CL 2014002198 A1 CL2014002198 A1 CL 2014002198A1 CL 2014002198 A CL2014002198 A CL 2014002198A CL 2014002198 A CL2014002198 A CL 2014002198A CL 2014002198 A1 CL2014002198 A1 CL 2014002198A1
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CL
Chile
Prior art keywords
aav
adeno
organs
tissues
cells
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CL2014002198A
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English (en)
Inventor
Katherine A High
Federico Mingozzi
Junwei Sun
Philip Johnson
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Philadelphia Children Hospital
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First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=48984822&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=CL2014002198(A1) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Philadelphia Children Hospital filed Critical Philadelphia Children Hospital
Publication of CL2014002198A1 publication Critical patent/CL2014002198A1/es

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    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/63Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79Vectors or expression systems specially adapted for eukaryotic hosts
    • C12N15/85Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
    • C12N15/86Viral vectors
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P7/00Drugs for disorders of the blood or the extracellular fluid
    • A61P7/04Antihaemorrhagics; Procoagulants; Haemostatic agents; Antifibrinolytic agents
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector

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  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Genetics & Genomics (AREA)
  • Engineering & Computer Science (AREA)
  • Chemical & Material Sciences (AREA)
  • Organic Chemistry (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Biotechnology (AREA)
  • Wood Science & Technology (AREA)
  • Zoology (AREA)
  • General Engineering & Computer Science (AREA)
  • Biomedical Technology (AREA)
  • General Health & Medical Sciences (AREA)
  • Molecular Biology (AREA)
  • Biochemistry (AREA)
  • Microbiology (AREA)
  • Plant Pathology (AREA)
  • Virology (AREA)
  • Biophysics (AREA)
  • Physics & Mathematics (AREA)
  • Animal Behavior & Ethology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Medicinal Chemistry (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Diabetes (AREA)
  • Hematology (AREA)
  • Epidemiology (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
CL2014002198A 2012-02-17 2014-08-18 Composiciones de vector de virus adenoasociado (aav) y métodos para transferencia de genes a células, órganos y tejidos CL2014002198A1 (es)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201261600415P 2012-02-17 2012-02-17

Publications (1)

Publication Number Publication Date
CL2014002198A1 true CL2014002198A1 (es) 2015-03-13

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ID=48984822

Family Applications (1)

Application Number Title Priority Date Filing Date
CL2014002198A CL2014002198A1 (es) 2012-02-17 2014-08-18 Composiciones de vector de virus adenoasociado (aav) y métodos para transferencia de genes a células, órganos y tejidos

Country Status (16)

Country Link
US (2) US20150111955A1 (es)
EP (1) EP2814958B1 (es)
JP (2) JP6373763B2 (es)
KR (1) KR102057540B1 (es)
CN (1) CN104520428B (es)
AU (1) AU2013221212B2 (es)
BR (1) BR112014020325A2 (es)
CA (1) CA2864879C (es)
CL (1) CL2014002198A1 (es)
ES (1) ES2752191T3 (es)
IL (1) IL234148B (es)
MX (1) MX367100B (es)
RU (1) RU2653444C2 (es)
SG (1) SG11201404956PA (es)
WO (1) WO2013123503A1 (es)
ZA (1) ZA201406065B (es)

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