JOP20190166A1 - استراتيجية مثلى من أجل تعديلات تخطي إكسون باستخدام crispr/cas9 مع متواليات توجيه ثلاثي - Google Patents

استراتيجية مثلى من أجل تعديلات تخطي إكسون باستخدام crispr/cas9 مع متواليات توجيه ثلاثي

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Publication number
JOP20190166A1
JOP20190166A1 JOP/2019/0166A JOP20190166A JOP20190166A1 JO P20190166 A1 JOP20190166 A1 JO P20190166A1 JO P20190166 A JOP20190166 A JO P20190166A JO P20190166 A1 JOP20190166 A1 JO P20190166A1
Authority
JO
Jordan
Prior art keywords
cas9
crispr
modifications
exon skipping
guide sequences
Prior art date
Application number
JOP/2019/0166A
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English (en)
Inventor
Leonela Amoasii
Eric Olson
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Univ Texas
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
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Publication date
Application filed by Univ Texas filed Critical Univ Texas
Publication of JOP20190166A1 publication Critical patent/JOP20190166A1/ar

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Abstract

غير متوفر
JOP/2019/0166A 2017-01-05 2017-06-16 استراتيجية مثلى من أجل تعديلات تخطي إكسون باستخدام crispr/cas9 مع متواليات توجيه ثلاثي JOP20190166A1 (ar)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201762442606P 2017-01-05 2017-01-05
US201762544449P 2017-08-11 2017-08-11
US201762596298P 2017-12-08 2017-12-08

Publications (1)

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JOP20190166A1 true JOP20190166A1 (ar) 2019-07-02

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Country Link
US (1) US20190338311A1 (ar)
EP (1) EP3565897B1 (ar)
JP (1) JP2020503869A (ar)
KR (1) KR102606174B1 (ar)
CN (1) CN110506115A (ar)
AU (1) AU2018205521A1 (ar)
BR (1) BR112019013962A2 (ar)
CA (1) CA3048635A1 (ar)
CL (1) CL2019001882A1 (ar)
CO (1) CO2019008181A2 (ar)
CR (1) CR20190326A (ar)
DK (1) DK3565897T3 (ar)
DO (1) DOP2019000179A (ar)
EC (1) ECSP19056408A (ar)
IL (1) IL267786A (ar)
JO (1) JOP20190166A1 (ar)
MA (1) MA47239A (ar)
MX (1) MX2019008064A (ar)
PE (1) PE20191357A1 (ar)
PH (1) PH12019501561A1 (ar)
SG (1) SG11201906147VA (ar)
WO (1) WO2018129296A1 (ar)

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