JP2016501531A - 配列操作および治療適用のための系、方法および組成物の送達、エンジニアリングおよび最適化 - Google Patents

配列操作および治療適用のための系、方法および組成物の送達、エンジニアリングおよび最適化 Download PDF

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JP2016501531A
JP2016501531A JP2015547543A JP2015547543A JP2016501531A JP 2016501531 A JP2016501531 A JP 2016501531A JP 2015547543 A JP2015547543 A JP 2015547543A JP 2015547543 A JP2015547543 A JP 2015547543A JP 2016501531 A JP2016501531 A JP 2016501531A
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sequence
crispr
target
tracr
polynucleotide
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JP2016501531A5 (2
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フェン・ジャン
マティアス・ハイデンライク
フェイ・ラン
ウーカシュ・スウィーチ
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Broad Institute Inc
Harvard University
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Broad Institute Inc
Harvard University
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AU2022203759A1 (en) 2022-06-23
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US20250382642A1 (en) 2025-12-18
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