MA49684A - Arnm modifié codant une glucose-6-phosphatase et utilisations associées - Google Patents
Arnm modifié codant une glucose-6-phosphatase et utilisations associéesInfo
- Publication number
- MA49684A MA49684A MA049684A MA49684A MA49684A MA 49684 A MA49684 A MA 49684A MA 049684 A MA049684 A MA 049684A MA 49684 A MA49684 A MA 49684A MA 49684 A MA49684 A MA 49684A
- Authority
- MA
- Morocco
- Prior art keywords
- glucose
- modified rna
- associated uses
- phosphatase
- phosphatase modified
- Prior art date
Links
- 102000003638 Glucose-6-Phosphatase Human genes 0.000 title 1
- 108010086800 Glucose-6-Phosphatase Proteins 0.000 title 1
Classifications
-
- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12Y—ENZYMES
- C12Y301/00—Hydrolases acting on ester bonds (3.1)
- C12Y301/03—Phosphoric monoester hydrolases (3.1.3)
- C12Y301/03009—Glucose-6-phosphatase (3.1.3.9)
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K38/00—Medicinal preparations containing peptides
- A61K38/16—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
- A61K38/43—Enzymes; Proenzymes; Derivatives thereof
- A61K38/46—Hydrolases (3)
- A61K38/465—Hydrolases (3) acting on ester bonds (3.1), e.g. lipases, ribonucleases
-
- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
- C12N9/00—Enzymes; Proenzymes; Compositions thereof; Processes for preparing, activating, inhibiting, separating or purifying enzymes
- C12N9/14—Hydrolases (3)
- C12N9/16—Hydrolases (3) acting on ester bonds (3.1)
Landscapes
- Health & Medical Sciences (AREA)
- Life Sciences & Earth Sciences (AREA)
- Chemical & Material Sciences (AREA)
- Organic Chemistry (AREA)
- Engineering & Computer Science (AREA)
- Bioinformatics & Cheminformatics (AREA)
- General Health & Medical Sciences (AREA)
- Zoology (AREA)
- Genetics & Genomics (AREA)
- Wood Science & Technology (AREA)
- Biochemistry (AREA)
- Medicinal Chemistry (AREA)
- General Engineering & Computer Science (AREA)
- Proteomics, Peptides & Aminoacids (AREA)
- Public Health (AREA)
- Veterinary Medicine (AREA)
- Animal Behavior & Ethology (AREA)
- Gastroenterology & Hepatology (AREA)
- Immunology (AREA)
- Pharmacology & Pharmacy (AREA)
- Epidemiology (AREA)
- Biotechnology (AREA)
- Microbiology (AREA)
- Biomedical Technology (AREA)
- Molecular Biology (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
Applications Claiming Priority (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762536000P | 2017-07-24 | 2017-07-24 |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| MA49684A true MA49684A (fr) | 2020-06-03 |
Family
ID=63143416
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| MA049684A MA49684A (fr) | 2017-07-24 | 2018-07-24 | Arnm modifié codant une glucose-6-phosphatase et utilisations associées |
Country Status (4)
| Country | Link |
|---|---|
| US (1) | US20200179494A1 (fr) |
| EP (1) | EP3658672A1 (fr) |
| MA (1) | MA49684A (fr) |
| WO (1) | WO2019023179A1 (fr) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| MX2021003015A (es) * | 2018-09-13 | 2021-07-15 | Modernatx Inc | Polinucleotidos que codifican glucosa-6-fosfatasa para el tratamiento de la glucogenosis. |
| US20230233475A1 (en) * | 2020-06-01 | 2023-07-27 | Modernatx, Inc. | Lipid nanoparticles containing polynucleotides encoding glucose-6-phosphatase and uses thereof |
| CN111972355A (zh) * | 2020-08-31 | 2020-11-24 | 中国医学科学院北京协和医院 | GSDIa型糖原累积症小鼠模型及其构建方法 |
| US20240207374A1 (en) * | 2021-03-24 | 2024-06-27 | Modernatx, Inc. | Lipid nanoparticles containing polynucleotides encoding glucose-6-phosphatase and uses thereof |
| WO2025165616A1 (fr) * | 2024-01-31 | 2025-08-07 | The Johns Hopkins University | Compositions et méthodes de traitement et de prévention du cancer |
Family Cites Families (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4485045A (en) | 1981-07-06 | 1984-11-27 | Research Corporation | Synthetic phosphatidyl cholines useful in forming liposomes |
| US4544545A (en) | 1983-06-20 | 1985-10-01 | Trustees University Of Massachusetts | Liposomes containing modified cholesterol for organ targeting |
| US5013556A (en) | 1989-10-20 | 1991-05-07 | Liposome Technology, Inc. | Liposomes with enhanced circulation time |
| PL2578685T3 (pl) | 2005-08-23 | 2020-01-31 | The Trustees Of The University Of Pennsylvania | Rna zawierający zmodyfikowane nukleozydy i sposoby jego zastosowania |
| BRPI0620316A2 (pt) | 2005-12-21 | 2011-11-08 | Wyeth Corp | formulações de proteìnas com viscosidades reduzida e seus usos |
| EP3318248B1 (fr) | 2009-12-01 | 2019-04-10 | Translate Bio, Inc. | Administration d'arnm pour l'augmentation des protéines et des enzymes dans des maladies génétiques humaines |
| US8853377B2 (en) | 2010-11-30 | 2014-10-07 | Shire Human Genetic Therapies, Inc. | mRNA for use in treatment of human genetic diseases |
| WO2012129648A1 (fr) | 2011-03-25 | 2012-10-04 | University Of Guelph | Activation d'expression de protéines de vecteurs de virus adéno-associés |
| US8916696B2 (en) * | 2011-06-12 | 2014-12-23 | City Of Hope | Aptamer-mRNA conjugates for targeted protein or peptide expression and methods for their use |
| CA3018046A1 (fr) | 2011-12-16 | 2013-06-20 | Moderna Therapeutics, Inc. | Nucleoside, nucleotide, et compositions d'acide nucleique modifies |
| WO2013151665A2 (fr) | 2012-04-02 | 2013-10-10 | modeRNA Therapeutics | Polynucléotides modifiés destinés à la production de protéines associées à une maladie humaine |
| EP2858679B2 (fr) | 2012-06-08 | 2024-06-05 | Translate Bio, Inc. | Administration pulmonaire d'arnm à des cellules cibles autres que pulmonaires |
| PL2922554T3 (pl) | 2012-11-26 | 2022-06-20 | Modernatx, Inc. | Na zmodyfikowany na końcach |
| ES3032935T3 (en) * | 2013-10-22 | 2025-07-29 | Translate Bio Inc | Lipid formulations for delivery of messenger rna |
| WO2015062738A1 (fr) * | 2013-11-01 | 2015-05-07 | Curevac Gmbh | Arn modifié à propriétés immunostimulantes réduites |
| US9850269B2 (en) * | 2014-04-25 | 2017-12-26 | Translate Bio, Inc. | Methods for purification of messenger RNA |
-
2018
- 2018-07-24 MA MA049684A patent/MA49684A/fr unknown
- 2018-07-24 EP EP18752382.4A patent/EP3658672A1/fr not_active Withdrawn
- 2018-07-24 US US16/631,585 patent/US20200179494A1/en not_active Abandoned
- 2018-07-24 WO PCT/US2018/043403 patent/WO2019023179A1/fr not_active Ceased
Also Published As
| Publication number | Publication date |
|---|---|
| WO2019023179A1 (fr) | 2019-01-31 |
| US20200179494A1 (en) | 2020-06-11 |
| EP3658672A1 (fr) | 2020-06-03 |
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