PL3182980T3 - Leczenie chorób niedoboru glikozylacji - Google Patents

Leczenie chorób niedoboru glikozylacji

Info

Publication number
PL3182980T3
PL3182980T3 PL15833822T PL15833822T PL3182980T3 PL 3182980 T3 PL3182980 T3 PL 3182980T3 PL 15833822 T PL15833822 T PL 15833822T PL 15833822 T PL15833822 T PL 15833822T PL 3182980 T3 PL3182980 T3 PL 3182980T3
Authority
PL
Poland
Prior art keywords
treatment
deficiency diseases
glycosylation deficiency
glycosylation
diseases
Prior art date
Application number
PL15833822T
Other languages
English (en)
Inventor
Reid W. Von Borstel
Original Assignee
Wellstat Therapeutics Corporation
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Wellstat Therapeutics Corporation filed Critical Wellstat Therapeutics Corporation
Publication of PL3182980T3 publication Critical patent/PL3182980T3/pl

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/70—Carbohydrates; Sugars; Derivatives thereof
    • A61K31/7042—Compounds having saccharide radicals and heterocyclic rings
    • A61K31/7052—Compounds having saccharide radicals and heterocyclic rings having nitrogen as a ring hetero atom, e.g. nucleosides, nucleotides
    • A61K31/706—Compounds having saccharide radicals and heterocyclic rings having nitrogen as a ring hetero atom, e.g. nucleosides, nucleotides containing six-membered rings with nitrogen as a ring hetero atom
    • A61K31/7064—Compounds having saccharide radicals and heterocyclic rings having nitrogen as a ring hetero atom, e.g. nucleosides, nucleotides containing six-membered rings with nitrogen as a ring hetero atom containing condensed or non-condensed pyrimidines
    • A61K31/7068—Compounds having saccharide radicals and heterocyclic rings having nitrogen as a ring hetero atom, e.g. nucleosides, nucleotides containing six-membered rings with nitrogen as a ring hetero atom containing condensed or non-condensed pyrimidines having oxo groups directly attached to the pyrimidine ring, e.g. cytidine, cytidylic acid
    • A61K31/7072—Compounds having saccharide radicals and heterocyclic rings having nitrogen as a ring hetero atom, e.g. nucleosides, nucleotides containing six-membered rings with nitrogen as a ring hetero atom containing condensed or non-condensed pyrimidines having oxo groups directly attached to the pyrimidine ring, e.g. cytidine, cytidylic acid having two oxo groups directly attached to the pyrimidine ring, e.g. uridine, uridylic acid, thymidine, zidovudine
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/70—Carbohydrates; Sugars; Derivatives thereof
    • A61K31/7004—Monosaccharides having only carbon, hydrogen and oxygen atoms
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/70—Carbohydrates; Sugars; Derivatives thereof
    • A61K31/7008—Compounds having an amino group directly attached to a carbon atom of the saccharide radical, e.g. D-galactosamine, ranimustine
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/70—Carbohydrates; Sugars; Derivatives thereof
    • A61K31/7012—Compounds having a free or esterified carboxyl group attached, directly or through a carbon chain, to a carbon atom of the saccharide radical, e.g. glucuronic acid, neuraminic acid
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K45/00—Medicinal preparations containing active ingredients not provided for in groups A61K31/00 - A61K41/00
    • A61K45/06—Mixtures of active ingredients without chemical characterisation, e.g. antiphlogistics and cardiaca
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Epidemiology (AREA)
  • Molecular Biology (AREA)
  • Engineering & Computer Science (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Organic Chemistry (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Neurology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
PL15833822T 2014-08-19 2015-08-19 Leczenie chorób niedoboru glikozylacji PL3182980T3 (pl)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201462039052P 2014-08-19 2014-08-19
EP15833822.8A EP3182980B1 (en) 2014-08-19 2015-08-19 Treatment of glycosylation deficiency diseases
PCT/US2015/045896 WO2016028894A1 (en) 2014-08-19 2015-08-19 Treatment of glycosylation deficiency diseases

Publications (1)

Publication Number Publication Date
PL3182980T3 true PL3182980T3 (pl) 2021-04-19

Family

ID=55351228

Family Applications (1)

Application Number Title Priority Date Filing Date
PL15833822T PL3182980T3 (pl) 2014-08-19 2015-08-19 Leczenie chorób niedoboru glikozylacji

Country Status (6)

Country Link
US (2) US20170209476A1 (pl)
EP (1) EP3182980B1 (pl)
DK (1) DK3182980T3 (pl)
ES (1) ES2841745T3 (pl)
PL (1) PL3182980T3 (pl)
WO (1) WO2016028894A1 (pl)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN118453508A (zh) * 2018-02-01 2024-08-09 维尔斯达医疗公司 包含尿苷的药物组合物及其应用以及用于递送尿苷的系统
US20220241311A1 (en) * 2018-06-14 2022-08-04 Mayo Foundation For Medical Education And Research Methods and materials for treating glycosylation disorders
IL300902A (en) * 2020-09-14 2023-04-01 Wellstat Therapeutics Corp 2',3'-diacetyluridine substituted with acetoacetyl at the 5' position
KR20230112118A (ko) * 2020-12-01 2023-07-26 웰스태트 테러퓨틱스 코포레이션 5'-o-페닐아세틸우리딘 및 치료 용도

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1808177B1 (en) * 1999-02-23 2018-08-08 The Regents of The University of California Methods of treatment of mitochondrial disorders
CA2632903C (en) * 2005-12-02 2015-11-24 Vianova Labs, Inc. Treatment of cancer and other diseases
WO2010132434A1 (en) * 2009-05-13 2010-11-18 Wellstat Therapeutics Corporation Determining the severity of 5-fluorouracil overdose
US20110257233A1 (en) * 2010-03-19 2011-10-20 Sanford-Burnham Medical Research Institute Benzoisothiazolones as inhibitors of phosphomannose isomerase
WO2013102904A1 (en) * 2012-01-05 2013-07-11 Hadasit Medical Research Services & Development Ltd. Methods and compositions for gene delivery

Also Published As

Publication number Publication date
EP3182980B1 (en) 2020-10-14
DK3182980T3 (da) 2021-01-11
US20220273688A1 (en) 2022-09-01
US20170209476A1 (en) 2017-07-27
EP3182980A1 (en) 2017-06-28
ES2841745T3 (es) 2021-07-09
WO2016028894A1 (en) 2016-02-25
EP3182980A4 (en) 2018-06-06

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