PL3298134T3 - Edycja genów mutacji głęboko intronowych - Google Patents

Edycja genów mutacji głęboko intronowych

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Publication number
PL3298134T3
PL3298134T3 PL16718840.8T PL16718840T PL3298134T3 PL 3298134 T3 PL3298134 T3 PL 3298134T3 PL 16718840 T PL16718840 T PL 16718840T PL 3298134 T3 PL3298134 T3 PL 3298134T3
Authority
PL
Poland
Prior art keywords
gene editing
deep intronic
intronic mutations
mutations
deep
Prior art date
Application number
PL16718840.8T
Other languages
English (en)
Inventor
Guoxiang RUAN
Abraham Scaria
Original Assignee
Genzyme Corporation
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Genzyme Corporation filed Critical Genzyme Corporation
Publication of PL3298134T3 publication Critical patent/PL3298134T3/pl

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PL16718840.8T 2015-05-16 2016-04-15 Edycja genów mutacji głęboko intronowych PL3298134T3 (pl)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201562162720P 2015-05-16 2015-05-16
PCT/US2016/027987 WO2016186772A2 (en) 2015-05-16 2016-04-15 Gene editing of deep intronic mutations

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PL3298134T3 true PL3298134T3 (pl) 2023-09-18

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US (2) US11896651B2 (pl)
EP (1) EP3298134B8 (pl)
JP (3) JP6985250B2 (pl)
KR (2) KR102584873B1 (pl)
CN (3) CN118879692A (pl)
AU (2) AU2016265255B2 (pl)
CA (1) CA2986021A1 (pl)
ES (1) ES2952598T3 (pl)
IL (2) IL296365A (pl)
MX (2) MX2017014665A (pl)
PL (1) PL3298134T3 (pl)
PT (1) PT3298134T (pl)
RU (2) RU2759335C2 (pl)
SG (2) SG10201910750WA (pl)
WO (1) WO2016186772A2 (pl)

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WO2013066438A2 (en) 2011-07-22 2013-05-10 President And Fellows Of Harvard College Evaluation and improvement of nuclease cleavage specificity
US9163284B2 (en) 2013-08-09 2015-10-20 President And Fellows Of Harvard College Methods for identifying a target site of a Cas9 nuclease
US9359599B2 (en) 2013-08-22 2016-06-07 President And Fellows Of Harvard College Engineered transcription activator-like effector (TALE) domains and uses thereof
US9322037B2 (en) 2013-09-06 2016-04-26 President And Fellows Of Harvard College Cas9-FokI fusion proteins and uses thereof
US9526784B2 (en) 2013-09-06 2016-12-27 President And Fellows Of Harvard College Delivery system for functional nucleases
US9340799B2 (en) 2013-09-06 2016-05-17 President And Fellows Of Harvard College MRNA-sensing switchable gRNAs
US20150166984A1 (en) 2013-12-12 2015-06-18 President And Fellows Of Harvard College Methods for correcting alpha-antitrypsin point mutations
US11028388B2 (en) 2014-03-05 2021-06-08 Editas Medicine, Inc. CRISPR/Cas-related methods and compositions for treating Usher syndrome and retinitis pigmentosa
US11141493B2 (en) 2014-03-10 2021-10-12 Editas Medicine, Inc. Compositions and methods for treating CEP290-associated disease
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