DK4285902T3 - Forstærket syre-alfa-glucosidase til behandling af pompes sygdom - Google Patents

Forstærket syre-alfa-glucosidase til behandling af pompes sygdom

Info

Publication number
DK4285902T3
DK4285902T3 DK23188938.7T DK23188938T DK4285902T3 DK 4285902 T3 DK4285902 T3 DK 4285902T3 DK 23188938 T DK23188938 T DK 23188938T DK 4285902 T3 DK4285902 T3 DK 4285902T3
Authority
DK
Denmark
Prior art keywords
glucosidase
disease
pump
treatment
acid alpha
Prior art date
Application number
DK23188938.7T
Other languages
English (en)
Inventor
Hung V Do
Richie Khanna
Russell Gotschall
Original Assignee
Amicus Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Amicus Therapeutics Inc filed Critical Amicus Therapeutics Inc
Application granted granted Critical
Publication of DK4285902T3 publication Critical patent/DK4285902T3/da

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00—Medicinal preparations containing peptides
    • A61K38/16—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • A61K38/43—Enzymes; Proenzymes; Derivatives thereof
    • A61K38/46—Hydrolases (3)
    • A61K38/47—Hydrolases (3) acting on glycosyl compounds (3.2), e.g. cellulases, lactases
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/33—Heterocyclic compounds
    • A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445—Non condensed piperidines, e.g. piperocaine
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12Y—ENZYMES
    • C12Y302/00—Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
    • C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/0102—Alpha-glucosidase (3.2.1.20)

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Engineering & Computer Science (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Animal Behavior & Ethology (AREA)
  • Organic Chemistry (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Epidemiology (AREA)
  • Zoology (AREA)
  • Immunology (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Wood Science & Technology (AREA)
  • Genetics & Genomics (AREA)
  • Biochemistry (AREA)
  • General Engineering & Computer Science (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Medicinal Preparation (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Immobilizing And Processing Of Enzymes And Microorganisms (AREA)
DK23188938.7T 2015-12-30 2016-12-29 Forstærket syre-alfa-glucosidase til behandling af pompes sygdom DK4285902T3 (da)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201562272890P 2015-12-30 2015-12-30
US201662300479P 2016-02-26 2016-02-26
US201662315412P 2016-03-30 2016-03-30
US201662402454P 2016-09-30 2016-09-30
US201662428867P 2016-12-01 2016-12-01
US201662431791P 2016-12-08 2016-12-08
EP21174249.9A EP3957320B1 (en) 2015-12-30 2016-12-29 Augmented acid alpha-glucosidase for the treatment of pompe disease

Publications (1)

Publication Number Publication Date
DK4285902T3 true DK4285902T3 (da) 2026-02-16

Family

ID=60186557

Family Applications (3)

Application Number Title Priority Date Filing Date
DK16826898.5T DK3397273T3 (da) 2015-12-30 2016-12-29 Forstærket syre-alfa-glucosidase til behandling af pompes sygdom
DK23188938.7T DK4285902T3 (da) 2015-12-30 2016-12-29 Forstærket syre-alfa-glucosidase til behandling af pompes sygdom
DK21174249.9T DK3957320T5 (da) 2015-12-30 2016-12-29 Forstærket syre-alfa-glucosidase til behandling af pompes sygdom

Family Applications Before (1)

Application Number Title Priority Date Filing Date
DK16826898.5T DK3397273T3 (da) 2015-12-30 2016-12-29 Forstærket syre-alfa-glucosidase til behandling af pompes sygdom

Family Applications After (1)

Application Number Title Priority Date Filing Date
DK21174249.9T DK3957320T5 (da) 2015-12-30 2016-12-29 Forstærket syre-alfa-glucosidase til behandling af pompes sygdom

Country Status (16)

Country Link
EP (4) EP4706779A2 (da)
CN (1) CN108472340A (da)
CY (1) CY1124637T1 (da)
DK (3) DK3397273T3 (da)
ES (3) ES2883844T3 (da)
FI (2) FI4285902T3 (da)
HK (1) HK1253014A1 (da)
HR (3) HRP20231465T1 (da)
HU (2) HUE054733T2 (da)
LT (3) LT3397273T (da)
PL (3) PL4285902T3 (da)
PT (3) PT3397273T (da)
RS (3) RS64843B1 (da)
SI (3) SI4285902T1 (da)
SM (3) SMT202100452T1 (da)
TW (3) TW202506173A (da)

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7723296B2 (en) * 2001-01-18 2010-05-25 Genzyme Corporation Methods for introducing mannose-6-phosphate and other oligosaccharides onto glycoproteins and its application thereof
PT2857036T (pt) 2003-01-31 2017-03-13 Mount Sinai School Of Medicine Of N Y Univ Terapia combinada para o tratamento de distúrbios de deficiência proteica
CA2553955C (en) * 2004-02-10 2012-08-28 Zystor Therapeutics, Inc. Acid alpha-glucosidase and fragments thereof
AU2006247065B8 (en) 2005-05-17 2012-07-12 Amicus Therapeutics, Inc. A method for the treatment of Pompe disease using 1-deoxynojirimycin derivatives
WO2009102895A2 (en) 2008-02-12 2009-08-20 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
WO2010138608A1 (en) * 2009-05-26 2010-12-02 Amicus Therapeutics, Inc. Utilization of pharmacological chaperones to improve manufacturing and purification of biologics
EP2844279B1 (en) 2012-05-03 2020-12-09 Amicus Therapeutics, Inc. Dosing regimens for the treatment of pompe disease
HK1209625A1 (en) 2012-07-17 2016-04-08 Amicus Therapeutics, Inc. Alpha-galactosidase a and 1-deoxygalactonojirimycin co-formulation
CN114540327B (zh) * 2014-09-30 2026-03-24 阿米库斯治疗学公司 具有增强的碳水化合物的高强度酸性α-葡糖苷酶

Also Published As

Publication number Publication date
EP3957320A1 (en) 2022-02-23
DK3957320T3 (da) 2023-11-27
EP3397273A1 (en) 2018-11-07
DK3397273T3 (da) 2021-08-09
TW202245831A (zh) 2022-12-01
EP3397273B1 (en) 2021-05-19
TWI849380B (zh) 2024-07-21
EP4706779A2 (en) 2026-03-11
TW202506173A (zh) 2025-02-16
TWI753874B (zh) 2022-02-01
SMT202600054T1 (it) 2026-03-09
PL4285902T3 (pl) 2026-04-13
LT3397273T (lt) 2021-06-25
HUE064049T2 (hu) 2024-02-28
FI4285902T3 (fi) 2026-02-17
SI3957320T1 (sl) 2024-01-31
FI3957320T3 (fi) 2023-11-23
HRP20260120T1 (hr) 2026-03-13
CY1124637T1 (el) 2022-07-22
HRP20231465T1 (hr) 2024-03-01
EP3957320B1 (en) 2023-08-23
PL3397273T3 (pl) 2021-12-06
DK3957320T5 (da) 2024-08-05
LT4285902T (lt) 2026-02-25
CN108472340A (zh) 2018-08-31
TW201726163A (zh) 2017-08-01
HK1253014A1 (zh) 2019-06-06
SMT202300412T1 (it) 2024-01-10
PT3957320T (pt) 2023-11-23
RS62212B1 (sr) 2021-09-30
PT4285902T (pt) 2026-02-10
RS67727B1 (sr) 2026-03-31
HRP20210894T1 (hr) 2021-07-23
SMT202100452T1 (it) 2021-09-14
RS64843B1 (sr) 2023-12-29
EP4285902B1 (en) 2025-11-19
HUE054733T2 (hu) 2021-09-28
ES3063549T3 (en) 2026-04-17
SI3397273T1 (sl) 2021-11-30
PL3957320T3 (pl) 2024-02-19
EP4285902A2 (en) 2023-12-06
EP4285902A3 (en) 2024-02-21
PT3397273T (pt) 2021-08-09
ES2965190T3 (es) 2024-04-11
ES2883844T3 (es) 2021-12-09
LT3957320T (lt) 2023-12-11
SI4285902T1 (sl) 2026-04-30

Similar Documents

Publication Publication Date Title
IL283837A (en) Augmented acid alpha-glucosidase for the treatment of pompe disease
LT3334422T (lt) Kanabidiolio rūgšties panaudojimas epilepsijos gydymui
DK3386511T3 (da) Fremgangsmåder til behandling af huntingtons sygdom
DK3516060T3 (da) Antisense-oligonukleotider til behandling af øjensygdom
EP3263132C0 (en) COMPOSITION FOR THE TREATMENT OF DISEASES ASSOCIATED WITH IL-6
DK3364997T5 (da) Aspartoacylase genterapi til behandling af canavans sygdom
DK3240612T3 (da) Fremgangsmåder til behandling af nethindesygdomme
IL247111A0 (en) Preventive or therapeutic agent for kidney disease
DK3294345T3 (da) Tpp1-formuleringer og fremgangsmåder til behandling af cln2-sygdom
HUE060517T2 (hu) Immunhiányos betegség kezelésére szolgáló eljárások
DK3452100T3 (da) FARMACEUTISKE BÆRERE INDEHOLDENDE miRNAer TIL ANVENDELSE I BEHANDLINGEN AF FIBROTISKE SYGDOMME FORÅRSAGET AF HYPERGLYKÆMI
EP3303556C0 (en) COMPOSITIONS FOR THE TREATMENT OF OSTEO-CARTILAGINOUS DISORDERS
DK3373931T3 (da) Heterocykliske forbindelser til behandling af sygdom
FR3058067B1 (fr) Systeme d'assistance circulatoire
DE112015002229A5 (de) Formulierungen zur Behandlung von Hyperthyreose
BR112016015712A2 (pt) método de tratamento de doenças hepáticas.
DK3406258T3 (da) Medikament til anvendelse til behandling af urinsyregigt
KR101583452B9 (ko) 위장질환 치료용 의약 조성물
ME03056B (me) Jedinjenja 3,4-diamino-6-hloropirazin-2-karboksamida za tretman bolesti posredovanih sa enac
DK3957320T5 (da) Forstærket syre-alfa-glucosidase til behandling af pompes sygdom
DK3423081T3 (da) Sammensætninger til brug i behandlingen af neurologisk sygdom
DK3072509T3 (da) Sammensætninger til behandling af mortellaros sygdom og fremgangsmåder til fremstilling deraf
LT3148588T (lt) N,n-bis-2-merkaptoetilizoftalamidas, skirtas parkinsono ligos gydymui
DK3393583T3 (da) Opløslig glycoprotein til behandling af trombotiske sygdomme