LT3624831T - Rekombinantinė žmogaus rūgštinė alfa-glukozidazė - Google Patents

Rekombinantinė žmogaus rūgštinė alfa-glukozidazė

Info

Publication number
LT3624831T
LT3624831T LTEPPCT/US2018/032815T LT18032815T LT3624831T LT 3624831 T LT3624831 T LT 3624831T LT 18032815 T LT18032815 T LT 18032815T LT 3624831 T LT3624831 T LT 3624831T
Authority
LT
Lithuania
Prior art keywords
glucosidase
recombinant human
acid alpha
human acid
alpha
Prior art date
Application number
LTEPPCT/US2018/032815T
Other languages
English (en)
Inventor
Hung Do
Russell GOTSCHALL
Richie Khanna
Yi Lun
Hing CHAR
Sergey TESLER
Wendy SUNDERLAND
Enrique DILONÉ
Original Assignee
Amicus Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Amicus Therapeutics, Inc. filed Critical Amicus Therapeutics, Inc.
Publication of LT3624831T publication Critical patent/LT3624831T/lt

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00—Medicinal preparations containing peptides
    • A61K38/16—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • A61K38/43—Enzymes; Proenzymes; Derivatives thereof
    • A61K38/46—Hydrolases (3)
    • A61K38/47—Hydrolases (3) acting on glycosyl compounds (3.2), e.g. cellulases, lactases
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P25/00—Drugs for disorders of the nervous system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12Y—ENZYMES
    • C12Y302/00—Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
    • C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/0102—Alpha-glucosidase (3.2.1.20)

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Organic Chemistry (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Animal Behavior & Ethology (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Neurology (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Immunology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Epidemiology (AREA)
  • Biochemistry (AREA)
  • General Engineering & Computer Science (AREA)
  • Zoology (AREA)
  • Genetics & Genomics (AREA)
  • Wood Science & Technology (AREA)
  • Biomedical Technology (AREA)
  • Neurosurgery (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Medicinal Preparation (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
LTEPPCT/US2018/032815T 2017-05-15 2018-05-15 Rekombinantinė žmogaus rūgštinė alfa-glukozidazė LT3624831T (lt)

Applications Claiming Priority (10)

Application Number Priority Date Filing Date Title
US201762506574P 2017-05-15 2017-05-15
US201762506561P 2017-05-15 2017-05-15
US201762506569P 2017-05-15 2017-05-15
US201762529300P 2017-07-06 2017-07-06
US201762564083P 2017-09-27 2017-09-27
US201762567334P 2017-10-03 2017-10-03
US201862618021P 2018-01-16 2018-01-16
US201862624638P 2018-01-31 2018-01-31
US201862660758P 2018-04-20 2018-04-20
PCT/US2018/032815 WO2018213340A1 (en) 2017-05-15 2018-05-15 Recombinant human acid alpha-glucosidase

Publications (1)

Publication Number Publication Date
LT3624831T true LT3624831T (lt) 2023-07-10

Family

ID=64274660

Family Applications (1)

Application Number Title Priority Date Filing Date
LTEPPCT/US2018/032815T LT3624831T (lt) 2017-05-15 2018-05-15 Rekombinantinė žmogaus rūgštinė alfa-glukozidazė

Country Status (25)

Country Link
US (2) US12246062B2 (lt)
EP (2) EP4223310A3 (lt)
JP (3) JP7193476B2 (lt)
KR (2) KR20250044950A (lt)
CN (3) CN119113091A (lt)
AU (2) AU2018270925B2 (lt)
BR (1) BR112019024125A2 (lt)
CA (1) CA3063615A1 (lt)
CL (1) CL2019003251A1 (lt)
DK (1) DK3624831T5 (lt)
ES (1) ES2950808T3 (lt)
FI (1) FI3624831T3 (lt)
HR (1) HRP20230576T1 (lt)
HU (1) HUE062504T2 (lt)
IL (2) IL270530B2 (lt)
LT (1) LT3624831T (lt)
MX (3) MX2019013624A (lt)
PL (1) PL3624831T3 (lt)
PT (1) PT3624831T (lt)
RS (1) RS64301B1 (lt)
SI (1) SI3624831T1 (lt)
SM (1) SMT202300187T1 (lt)
TW (2) TW202448499A (lt)
WO (1) WO2018213340A1 (lt)
ZA (1) ZA201907552B (lt)

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SG11201808455VA (en) 2016-03-30 2018-10-30 Amicus Therapeutics Inc Formulations comprising recombinant acid alpha-glucosidase
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BR112020023145A2 (pt) 2018-05-17 2021-02-02 Regeneron Pharmaceuticals, Inc. anticorpo anti-cd63 ou fragmento de ligação ao antígeno do mesmo, molécula de ligação ao antígeno biespecífica, proteína terapêutica de múltiplos domínios, polinucleotídeo composição farmacêutica, e, composto
US12018087B2 (en) 2018-08-02 2024-06-25 Dyne Therapeutics, Inc. Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject
EP3871687A1 (en) * 2020-02-27 2021-09-01 eleva GmbH Enzyme replacement therapy for treating pompe disease
US20240197839A1 (en) * 2021-02-11 2024-06-20 Amicus Therapeutics, Inc. Recombinant Human Acid Alpha-Glucosidase and Uses Thereof
CN114280182A (zh) * 2021-12-23 2022-04-05 福建省中医药科学院 一种太子参均一多糖的hplc-fld检测方法
US20250134967A1 (en) * 2022-02-07 2025-05-01 M6P Therapeutics, Inc. Compositions comprising acid alpha glucosidase and methods of use thereof
AU2023265155A1 (en) * 2022-05-05 2024-12-12 Amicus Therapeutics, Inc. Methods for treating pompe disease
EP4626464A1 (en) * 2022-12-02 2025-10-08 Amicus Therapeutics, Inc. Fexamethods for treating infantile-onset pompe disease in pediatric patients
KR20250113510A (ko) * 2022-12-02 2025-07-25 아미쿠스 세라퓨틱스, 인코포레이티드 소아 환자의 후기 발병 폼페병 치료에 대한 방법
WO2026004963A1 (ja) * 2024-06-26 2026-01-02 三菱ケミカル株式会社 分離材、分離材の製造方法、標的分子の分離方法、混合物、及びクロマトグラフィー用カラム

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Also Published As

Publication number Publication date
EP3624831A4 (en) 2021-02-17
RS64301B1 (sr) 2023-07-31
PL3624831T3 (pl) 2023-08-14
ES2950808T3 (es) 2023-10-13
EP3624831B1 (en) 2023-03-29
DK3624831T5 (da) 2024-09-02
ZA201907552B (en) 2024-09-25
WO2018213340A1 (en) 2018-11-22
EP4223310A2 (en) 2023-08-09
IL310719A (en) 2024-04-01
PT3624831T (pt) 2023-07-04
CA3063615A1 (en) 2018-11-22
EP3624831A1 (en) 2020-03-25
HUE062504T2 (hu) 2023-11-28
EP4223310A3 (en) 2023-10-11
MX2024015740A (es) 2025-02-10
CN119139461A (zh) 2024-12-17
HRP20230576T1 (hr) 2023-09-01
JP2020519638A (ja) 2020-07-02
US20210393747A1 (en) 2021-12-23
CN119113091A (zh) 2024-12-13
IL270530B1 (en) 2024-03-01
US20250057925A1 (en) 2025-02-20
KR20200004414A (ko) 2020-01-13
TWI870336B (zh) 2025-01-21
KR102787774B1 (ko) 2025-04-01
SI3624831T1 (sl) 2023-08-31
BR112019024125A2 (pt) 2020-06-02
DK3624831T3 (da) 2023-06-26
IL270530A (en) 2020-01-30
JP7193476B2 (ja) 2022-12-20
MX2019013624A (es) 2020-01-13
AU2025203557A1 (en) 2025-06-05
CN111356474A (zh) 2020-06-30
TW202448499A (zh) 2024-12-16
TW201900208A (zh) 2019-01-01
AU2018270925B2 (en) 2025-02-20
KR20250044950A (ko) 2025-04-01
SMT202300187T1 (it) 2023-07-20
AU2018270925A1 (en) 2019-11-28
CL2019003251A1 (es) 2020-05-22
US12246062B2 (en) 2025-03-11
IL270530B2 (en) 2024-07-01
JP2023051927A (ja) 2023-04-11
FI3624831T3 (fi) 2023-06-12
MX2024015741A (es) 2025-02-10
JP2025016455A (ja) 2025-02-04

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