PL3386484T3 - Kompozycje i sposoby dostarczania środków terapeutycznych - Google Patents

Kompozycje i sposoby dostarczania środków terapeutycznych

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Publication number
PL3386484T3
PL3386484T3 PL16873489.5T PL16873489T PL3386484T3 PL 3386484 T3 PL3386484 T3 PL 3386484T3 PL 16873489 T PL16873489 T PL 16873489T PL 3386484 T3 PL3386484 T3 PL 3386484T3
Authority
PL
Poland
Prior art keywords
delivery
compositions
methods
therapeutic agents
therapeutic
Prior art date
Application number
PL16873489.5T
Other languages
English (en)
Inventor
Gilles BESIN
Stephen Hoge
Joseph Senn
Kerry BENENATO
Staci SABNIS
Original Assignee
Modernatx, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Modernatx, Inc. filed Critical Modernatx, Inc.
Publication of PL3386484T3 publication Critical patent/PL3386484T3/pl

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    • A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
    • A61K48/0025—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid
    • A61K48/0033—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid the non-active part being non-polymeric
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