PT4062916T - Tratamento de pacientes com fabry com mutações específicas - Google Patents

Tratamento de pacientes com fabry com mutações específicas

Info

Publication number
PT4062916T
PT4062916T PT221656697T PT22165669T PT4062916T PT 4062916 T PT4062916 T PT 4062916T PT 221656697 T PT221656697 T PT 221656697T PT 22165669 T PT22165669 T PT 22165669T PT 4062916 T PT4062916 T PT 4062916T
Authority
PT
Portugal
Prior art keywords
methods
renal impairment
fabry patients
treating fabry
treating
Prior art date
Application number
PT221656697T
Other languages
English (en)
Original Assignee
Amicus Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=65803261&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=PT4062916(T) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Amicus Therapeutics Inc filed Critical Amicus Therapeutics Inc
Publication of PT4062916T publication Critical patent/PT4062916T/pt

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445Non condensed piperidines, e.g. piperocaine
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P13/00Drugs for disorders of the urinary system
    • A61P13/12Drugs for disorders of the urinary system of the kidneys
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12YENZYMES
    • C12Y302/00Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
    • C12Y302/01Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/01022Alpha-galactosidase (3.2.1.22)

Landscapes

  • Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Animal Behavior & Ethology (AREA)
  • Organic Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Medicinal Chemistry (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Urology & Nephrology (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Epidemiology (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Engineering & Computer Science (AREA)
  • Genetics & Genomics (AREA)
  • Wood Science & Technology (AREA)
  • Biochemistry (AREA)
  • Zoology (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
PT221656697T 2017-05-30 2018-05-30 Tratamento de pacientes com fabry com mutações específicas PT4062916T (pt)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201762512458P 2017-05-30 2017-05-30
US201862626953P 2018-02-06 2018-02-06

Publications (1)

Publication Number Publication Date
PT4062916T true PT4062916T (pt) 2025-01-13

Family

ID=65803261

Family Applications (4)

Application Number Title Priority Date Filing Date
PT187334156T PT3630114T (pt) 2017-05-30 2018-05-30 Migalastato para tratamento de pacientes com fabry com deficiência renal
PT232199331T PT4327869T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal
PT232199497T PT4324522T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal
PT221656697T PT4062916T (pt) 2017-05-30 2018-05-30 Tratamento de pacientes com fabry com mutações específicas

Family Applications Before (3)

Application Number Title Priority Date Filing Date
PT187334156T PT3630114T (pt) 2017-05-30 2018-05-30 Migalastato para tratamento de pacientes com fabry com deficiência renal
PT232199331T PT4327869T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal
PT232199497T PT4324522T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal

Country Status (14)

Country Link
EP (9) EP4062916B1 (pt)
CN (4) CN111278438A (pt)
DK (4) DK4062916T3 (pt)
ES (3) ES2970419T3 (pt)
FI (4) FI4062916T3 (pt)
HR (4) HRP20240061T1 (pt)
HU (2) HUE065615T2 (pt)
LT (4) LT4324522T (pt)
PL (4) PL4062916T3 (pt)
PT (4) PT3630114T (pt)
RS (3) RS65230B1 (pt)
SI (2) SI3630114T1 (pt)
SM (2) SMT202500016T1 (pt)
TW (4) TW202322814A (pt)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2021015352A (es) * 2019-06-11 2022-04-06 Amicus Therapeutics Inc Métodos para tratar la enfermedad de fabry en pacientes que tienen insuficiencia renal.
KR20220044560A (ko) * 2019-08-07 2022-04-08 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
PL2533050T6 (pl) * 2006-05-16 2016-05-31 Amicus Therapeutics Inc Możliwości leczenia choroby Fabry'ego
MX2009010557A (es) 2007-03-30 2009-11-19 Amicus Therapeutics Inc Metodo para el tratamiento de la enfermedad de fabry que utiliza chaperonas farmacologicas.
MX2009011473A (es) * 2007-04-26 2010-01-18 Amicus Therapeutics Inc Regimenes de dosificacion para el tratamiento de enfermedades por almacenamiento lisosomal que utilizan chaperonas farmacologicas.
US9999618B2 (en) * 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
EP2946785B1 (en) 2008-02-12 2018-10-24 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
SG10201604757RA (en) * 2011-03-11 2016-08-30 Amicus Therapeutics Inc Dosing regimens for the treatment of fabry disease
US20120283290A1 (en) * 2011-05-06 2012-11-08 Amicus Therapeutics Inc. Quantitation of gl3 in urine
TW202408513A (zh) 2016-07-19 2024-03-01 美商阿米庫斯醫療股份有限公司 治療ert初治的和已經歷ert的患者中之法布瑞氏症
CA3224546C (en) 2017-05-30 2026-02-24 Amicus Therapeutics, Inc. Use of migalastat in the treatment of fabry patients
SG11202000423XA (en) * 2017-07-19 2020-02-27 Amicus Therapeutics Inc Treatment of fabry disease in ert-naïve and ert-experienced patients

Also Published As

Publication number Publication date
EP4374918A3 (en) 2024-08-14
EP3630114B1 (en) 2023-11-01
LT3630114T (lt) 2024-02-12
HUE069837T2 (hu) 2025-04-28
HRP20241738T1 (hr) 2025-02-28
EP4327869A3 (en) 2024-05-22
PT4327869T (pt) 2026-03-12
DK3630114T3 (da) 2024-01-29
EP4374918B1 (en) 2025-07-16
FI3630114T3 (fi) 2024-01-30
LT4327869T (lt) 2026-03-25
TWI775453B (zh) 2022-08-21
EP4324522A2 (en) 2024-02-21
RS65230B1 (sr) 2024-03-29
EP4324522B1 (en) 2025-12-10
EP4324522A3 (en) 2024-05-22
LT4062916T (lt) 2025-01-10
SI3630114T1 (sl) 2024-03-29
PT3630114T (pt) 2024-02-01
EP4327869A2 (en) 2024-02-28
EP4635496A1 (en) 2025-10-22
RS67849B1 (sr) 2026-03-31
EP4327868A2 (en) 2024-02-28
TW202322814A (zh) 2023-06-16
SMT202400037T1 (it) 2024-03-13
EP4245366A9 (en) 2023-12-06
EP4062916B1 (en) 2024-10-09
CN117357524A (zh) 2024-01-09
CN119587544A (zh) 2025-03-11
FI4327869T3 (fi) 2026-03-09
PL4324522T3 (pl) 2026-04-27
HRP20260335T1 (hr) 2026-04-10
CN120732857A (zh) 2025-10-03
EP4374918A2 (en) 2024-05-29
ES2970419T3 (es) 2024-05-28
PL4327869T3 (pl) 2026-04-27
LT4324522T (lt) 2026-03-25
ES3052647T3 (en) 2026-01-12
TW201900165A (zh) 2019-01-01
FI4062916T3 (fi) 2025-01-10
HRP20260346T1 (hr) 2026-04-24
EP4062915A1 (en) 2022-09-28
EP3630114A1 (en) 2020-04-08
EP4327869B1 (en) 2025-12-10
FI4324522T3 (fi) 2026-03-09
SI4062916T1 (sl) 2025-04-30
HUE065615T2 (hu) 2024-06-28
DK4327869T3 (da) 2026-03-16
EP4245366A3 (en) 2023-11-29
ES3002433T3 (en) 2025-03-06
EP4062916A1 (en) 2022-09-28
TWI795408B (zh) 2023-03-11
TWI894750B (zh) 2025-08-21
TW202440104A (zh) 2024-10-16
RS66376B1 (sr) 2025-02-28
EP4245366A2 (en) 2023-09-20
PL4062916T3 (pl) 2025-03-17
CN111278438A (zh) 2020-06-12
PL3630114T3 (pl) 2024-03-25
HRP20240061T1 (hr) 2024-03-29
DK4062916T3 (da) 2025-01-13
TW202140000A (zh) 2021-11-01
DK4324522T3 (da) 2026-03-16
SMT202500016T1 (it) 2025-03-12
PT4324522T (pt) 2026-03-13

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