PT4062916T - Tratamento de pacientes com fabry com mutações específicas - Google Patents

Tratamento de pacientes com fabry com mutações específicas

Info

Publication number
PT4062916T
PT4062916T PT221656697T PT22165669T PT4062916T PT 4062916 T PT4062916 T PT 4062916T PT 221656697 T PT221656697 T PT 221656697T PT 22165669 T PT22165669 T PT 22165669T PT 4062916 T PT4062916 T PT 4062916T
Authority
PT
Portugal
Prior art keywords
methods
renal impairment
fabry patients
treating fabry
treating
Prior art date
Application number
PT221656697T
Other languages
English (en)
Original Assignee
Amicus Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=65803261&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=PT4062916(T) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Amicus Therapeutics Inc filed Critical Amicus Therapeutics Inc
Publication of PT4062916T publication Critical patent/PT4062916T/pt

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445Non condensed piperidines, e.g. piperocaine
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P13/00Drugs for disorders of the urinary system
    • A61P13/12Drugs for disorders of the urinary system of the kidneys
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12YENZYMES
    • C12Y302/00Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
    • C12Y302/01Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/01022Alpha-galactosidase (3.2.1.22)

Landscapes

  • Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Organic Chemistry (AREA)
  • Animal Behavior & Ethology (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Urology & Nephrology (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Epidemiology (AREA)
  • Genetics & Genomics (AREA)
  • General Engineering & Computer Science (AREA)
  • Biochemistry (AREA)
  • Wood Science & Technology (AREA)
  • Zoology (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
PT221656697T 2017-05-30 2018-05-30 Tratamento de pacientes com fabry com mutações específicas PT4062916T (pt)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201762512458P 2017-05-30 2017-05-30
US201862626953P 2018-02-06 2018-02-06

Publications (1)

Publication Number Publication Date
PT4062916T true PT4062916T (pt) 2025-01-13

Family

ID=65803261

Family Applications (4)

Application Number Title Priority Date Filing Date
PT232199497T PT4324522T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal
PT187334156T PT3630114T (pt) 2017-05-30 2018-05-30 Migalastato para tratamento de pacientes com fabry com deficiência renal
PT232199331T PT4327869T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal
PT221656697T PT4062916T (pt) 2017-05-30 2018-05-30 Tratamento de pacientes com fabry com mutações específicas

Family Applications Before (3)

Application Number Title Priority Date Filing Date
PT232199497T PT4324522T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal
PT187334156T PT3630114T (pt) 2017-05-30 2018-05-30 Migalastato para tratamento de pacientes com fabry com deficiência renal
PT232199331T PT4327869T (pt) 2017-05-30 2018-05-30 Métodos de tratamento de pacientes com fabry tendo insuficiência renal

Country Status (14)

Country Link
EP (9) EP4245366A3 (pt)
CN (4) CN117357524A (pt)
DK (4) DK4327869T3 (pt)
ES (5) ES3002433T3 (pt)
FI (4) FI4327869T3 (pt)
HR (4) HRP20240061T1 (pt)
HU (2) HUE069837T2 (pt)
LT (4) LT4324522T (pt)
PL (4) PL3630114T3 (pt)
PT (4) PT4324522T (pt)
RS (4) RS65230B1 (pt)
SI (2) SI4062916T1 (pt)
SM (4) SMT202600114T1 (pt)
TW (4) TW202322814A (pt)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
BR112021024886A2 (pt) * 2019-06-11 2022-01-25 Amicus Therapeutics Inc Métodos de tratar a doença de fabry em pacientes com insuficiência renal
WO2021026447A1 (en) * 2019-08-07 2021-02-11 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
JP2009537149A (ja) * 2006-05-16 2009-10-29 アミークス セラピューティックス インコーポレイテッド ファブリー病に対する治療の選択を診断し、評価するためのアッセイ
MX2009010557A (es) 2007-03-30 2009-11-19 Amicus Therapeutics Inc Metodo para el tratamiento de la enfermedad de fabry que utiliza chaperonas farmacologicas.
US9999618B2 (en) * 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
WO2008134628A2 (en) 2007-04-26 2008-11-06 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
WO2009102895A2 (en) * 2008-02-12 2009-08-20 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
US20140219986A1 (en) * 2011-03-11 2014-08-07 Amicus Therapeutics ,Inc. Dosing regimens for the treatment of fabry disease
US20120283290A1 (en) * 2011-05-06 2012-11-08 Amicus Therapeutics Inc. Quantitation of gl3 in urine
AU2017298376A1 (en) 2016-07-19 2019-03-07 Amicus Therapeutics, Inc. Treatment of Fabry disease in ERT-naive and ERT-experienced patients
KR20220116305A (ko) 2017-05-30 2022-08-22 아미쿠스 세라퓨틱스, 인코포레이티드 신장 손상을 갖는 파브리 환자를 치료하는 방법
WO2019017938A1 (en) * 2017-07-19 2019-01-24 Amicus Therapeutics, Inc. TREATMENT OF FABRY'S DISEASE IN PATIENTS WITHOUT SUBSTITUTED ENZYMATIC THERAPY (TES) AND PATIENTS SUBJECT TO TES

Also Published As

Publication number Publication date
FI4327869T3 (fi) 2026-03-09
LT4062916T (lt) 2025-01-10
TW202140000A (zh) 2021-11-01
EP4062916A1 (en) 2022-09-28
HRP20260346T1 (hr) 2026-04-24
FI4324522T3 (fi) 2026-03-09
FI3630114T3 (fi) 2024-01-30
RS67849B1 (sr) 2026-03-31
EP4327869A3 (en) 2024-05-22
EP4245366A9 (en) 2023-12-06
TWI775453B (zh) 2022-08-21
PL3630114T3 (pl) 2024-03-25
ES3065434T3 (en) 2026-05-06
TWI894750B (zh) 2025-08-21
CN111278438A (zh) 2020-06-12
EP4324522A3 (en) 2024-05-22
ES3052647T3 (en) 2026-01-12
HUE065615T2 (hu) 2024-06-28
RS66376B1 (sr) 2025-02-28
DK4062916T3 (da) 2025-01-13
EP3630114A1 (en) 2020-04-08
HRP20260335T1 (hr) 2026-04-10
DK3630114T3 (da) 2024-01-29
LT3630114T (lt) 2024-02-12
DK4324522T3 (da) 2026-03-16
ES2970419T3 (es) 2024-05-28
LT4327869T (lt) 2026-03-25
DK4327869T3 (da) 2026-03-16
PT4327869T (pt) 2026-03-12
PL4327869T3 (pl) 2026-04-27
TW202440104A (zh) 2024-10-16
RS67861B1 (sr) 2026-04-30
CN120732857A (zh) 2025-10-03
SMT202600114T1 (it) 2026-05-12
SMT202500016T1 (it) 2025-03-12
SMT202400037T1 (it) 2024-03-13
EP4327868A2 (en) 2024-02-28
FI4062916T3 (fi) 2025-01-10
ES3002433T3 (en) 2025-03-06
EP4324522B1 (en) 2025-12-10
HUE069837T2 (hu) 2025-04-28
TW202322814A (zh) 2023-06-16
CN117357524A (zh) 2024-01-09
SI4062916T1 (sl) 2025-04-30
PT4324522T (pt) 2026-03-13
EP4062916B1 (en) 2024-10-09
HRP20241738T1 (hr) 2025-02-28
EP4324522A2 (en) 2024-02-21
PL4062916T3 (pl) 2025-03-17
SMT202600113T1 (it) 2026-05-12
TWI795408B (zh) 2023-03-11
EP4635496A1 (en) 2025-10-22
ES3065413T3 (en) 2026-05-06
PL4324522T3 (pl) 2026-04-27
EP4245366A2 (en) 2023-09-20
EP3630114B9 (en) 2026-05-20
SI3630114T1 (sl) 2024-03-29
EP4374918A3 (en) 2024-08-14
EP4245366A3 (en) 2023-11-29
EP4327869B1 (en) 2025-12-10
EP3630114B1 (en) 2023-11-01
RS65230B1 (sr) 2024-03-29
PT3630114T (pt) 2024-02-01
EP4062915A1 (en) 2022-09-28
CN119587544A (zh) 2025-03-11
LT4324522T (lt) 2026-03-25
TW201900165A (zh) 2019-01-01
EP4374918B1 (en) 2025-07-16
EP4374918A2 (en) 2024-05-29
HRP20240061T1 (hr) 2024-03-29
EP4327869A2 (en) 2024-02-28

Similar Documents

Publication Publication Date Title
ZA202006746B (en) Methods of treatment
GB201804514D0 (en) Treatment of pyroptosis
GB201706406D0 (en) Method of treatment
EP3684342C0 (en) TREATMENT PROCEDURES
ZA201705997B (en) Method of preventing or treating hearing loss
GB201815588D0 (en) Method of treatment
ZA201705847B (en) Treatment of pain
GB201804515D0 (en) Treatment of necroptosis
SG11202102878TA (en) Treatment methods
SG11202102827YA (en) Treatment methods
SG11202005850VA (en) Methods of treatment of hypertrigl yceridemia
ES3065413T3 (en) Methods of treating fabry patients having renal impairment
GB201717555D0 (en) Blood filter
GB201801249D0 (en) Methods of treatment
GB201720439D0 (en) Method of treatment
GB201718589D0 (en) Method of treatment
GB201709554D0 (en) Method of treatment
GB201706642D0 (en) Method of treatment
GB201706452D0 (en) Method of treatment
GB201706404D0 (en) Method of treatment
GB201706398D0 (en) Method of treatment