DK3864152T3 - Fremgangsmåder og sammensætninger til editering af rna'er - Google Patents

Fremgangsmåder og sammensætninger til editering af rna'er Download PDF

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Publication number
DK3864152T3
DK3864152T3 DK19870299.5T DK19870299T DK3864152T3 DK 3864152 T3 DK3864152 T3 DK 3864152T3 DK 19870299 T DK19870299 T DK 19870299T DK 3864152 T3 DK3864152 T3 DK 3864152T3
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compositions
methods
rnas
editing
editing rnas
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DK19870299.5T
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DK3864152T5 (da
Inventor
Wensheng Wei
Liang Qu
Zongyi Yi
Shiyou Zhu
Chunhui Wang
Zhongzheng Cao
Zhuo Zhou
Pengfei Yuan
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Univ Beijing
Edigene Therapeutics Beijing Inc
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Application filed by Univ Beijing, Edigene Therapeutics Beijing Inc filed Critical Univ Beijing
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DK19870299.5T 2018-10-12 2019-10-12 Fremgangsmåder og sammensætninger til editering af rna'er DK3864152T5 (da)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
CN2018110105 2018-10-12
CN2019082713 2019-04-15
PCT/CN2019/110782 WO2020074001A1 (en) 2018-10-12 2019-10-12 Methods and Compositions for Editing RNAs

Publications (2)

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DK3864152T3 true DK3864152T3 (da) 2023-10-09
DK3864152T5 DK3864152T5 (da) 2024-08-12

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US (2) US20210355494A1 (da)
EP (3) EP3864152B1 (da)
JP (2) JP7252328B2 (da)
KR (1) KR102666695B1 (da)
CN (4) CN115651927B (da)
AU (2) AU2019357450B2 (da)
BR (1) BR112021006844A8 (da)
CA (1) CA3115864A1 (da)
CL (1) CL2021000880A1 (da)
CO (1) CO2021005956A2 (da)
CR (1) CR20210243A (da)
DK (1) DK3864152T5 (da)
EC (1) ECSP21033637A (da)
ES (1) ES2962434T3 (da)
IL (1) IL282191A (da)
MX (1) MX2021004187A (da)
PE (1) PE20211402A1 (da)
PH (1) PH12021550805A1 (da)
SG (1) SG11202103666PA (da)
TW (1) TW202028466A (da)
WO (1) WO2020074001A1 (da)

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EP3956449B1 (en) 2019-04-15 2026-02-25 EdiGene Therapeutics (Beijing) Inc. Methods and compositions for editing rnas
EP3997229A4 (en) 2019-07-12 2024-07-03 Peking University TARGETED RNA EDITING BY HARNESSING ENDOGENOUS ADAR USING MODIFIED RNA
AU2020395113A1 (en) 2019-12-02 2022-06-09 Shape Therapeutics Inc. Therapeutic editing
KR20220119129A (ko) 2019-12-30 2022-08-26 에디진 테라퓨틱스 (베이징) 인크. Leaper 기술에 기반한 mps ih 치료 방법 및 조성물
BR112022012921A2 (pt) 2019-12-30 2022-09-06 Edigene Therapeutics Beijing Inc Métodos para editar de forma alvejada ácido ribonucleico e para tratar a síndrome de usher tipo ii, ácido ribonucleico de recrutamento da adenosina desaminase, construto ou vetor de entrega, célula, e, uso do ácido ribonucleico de recrutamento da adenosina desaminase ou do construto ou vetor de entrega
AU2021257508A1 (en) * 2020-04-15 2022-11-17 Edigene Therapeutics (Beijing) Inc. Method and drug for treating Hurler syndrome
CN115777020A (zh) * 2020-04-22 2023-03-10 塑造治疗公司 使用snrna组分的组合物和方法
KR20230033651A (ko) * 2020-05-28 2023-03-08 코로 바이오, 인크. Serpina1의 adar-매개 편집을 위한 방법 및 조성물
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WO2022147573A1 (en) * 2021-01-04 2022-07-07 The Regents Of The University Of California Programmable rna editing in vivo via recruitment of endogenous adars
JP2024504608A (ja) * 2021-01-12 2024-02-01 北京大学 遺伝子操作ｒｎａを使用した内因性ａｄａｒの活用による標的化ｒｎａの編集
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US20250102522A1 (en) 2021-10-07 2025-03-27 Hepatx Corporation Methods of tracking donor cells in a recipient
MX2024004934A (es) * 2021-10-29 2024-09-10 Duke Univeristy Composiciones y sistemas para la edicion de celulas programables por arn y metodos para elaborar y usar los mismos.
WO2023143539A1 (en) * 2022-01-28 2023-08-03 Edigene Therapeutics (Beijing) Inc. Engineered adar-recruiting rnas and methods of use thereof
WO2023185231A1 (en) * 2022-04-02 2023-10-05 Edigene Therapeutics (Beijing) Inc. Engineered adar-recruiting rnas and methods of use for usher syndrome
US20260021204A1 (en) * 2022-07-15 2026-01-22 Georgia Tech Research Corporation Anti-sars-cov-1 and anti-sars-cov-2 activatable rnase guide sequences
AU2023364059A1 (en) * 2022-10-18 2025-05-08 Regeneron Pharmaceuticals, Inc. Compositions and methods comprising programmable snrnas for rna editing
US12565665B2 (en) 2022-12-21 2026-03-03 Trustees Of Boston University Compositions and methods for controlled mRNA translation and stability
CN118620958A (zh) * 2023-03-08 2024-09-10 广州医科大学 一种抗原表位的制备方法
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EP3864152B1 (en) * 2018-10-12 2023-08-16 Peking University Methods and compositions for editing rnas

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CN116218836A (zh) 2023-06-06
KR20210076082A (ko) 2021-06-23
CN116042611A (zh) 2023-05-02
MX2021004187A (es) 2021-09-08
CN115651927B (zh) 2023-06-16
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SG11202103666PA (en) 2021-05-28
CA3115864A1 (en) 2020-04-16
JP2023078373A (ja) 2023-06-06
EP3864152A4 (en) 2021-10-13
DK3864152T5 (da) 2024-08-12
ES2962434T3 (es) 2024-03-19
PE20211402A1 (es) 2021-08-02
EP4306116A3 (en) 2024-04-17
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WO2020074001A1 (en) 2020-04-16
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US20210310026A1 (en) 2021-10-07
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