JP2015518712A - Ｍｅｃｐ２発現を調節するための組成物及び方法 - Google Patents

Ｍｅｃｐ２発現を調節するための組成物及び方法 Download PDF

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JP2015518712A
JP2015518712A JP2015512847A JP2015512847A JP2015518712A JP 2015518712 A JP2015518712 A JP 2015518712A JP 2015512847 A JP2015512847 A JP 2015512847A JP 2015512847 A JP2015512847 A JP 2015512847A JP 2015518712 A JP2015518712 A JP 2015518712A
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nucleotide
oligonucleotide
stranded oligonucleotide
nucleotides
sequence
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JP2015518712A5 (2
Inventor
アーサー エム． クリーグ，
アーサー エム． クリーグ，
ロメシュ スブラマニアン，
ロメシュ スブラマニアン，
ジェイムズ マクスウィゲン，
ジェイムズ マクスウィゲン，
ジェニー ティー． リー，
ジェニー ティー． リー，
Original Assignee
ラナ セラピューティクス インコーポレイテッド
ラナ セラピューティクス インコーポレイテッド
ザ ジェネラル ホスピタル コーポレイション
ザ ジェネラル ホスピタル コーポレイション
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JP2015512847A 2012-05-16 2013-05-16 Ｍｅｃｐ２発現を調節するための組成物及び方法 Pending JP2015518712A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201261648051P 2012-05-16 2012-05-16
US61/648,051 2012-05-16
PCT/US2013/041394 WO2013173608A1 (en) 2012-05-16 2013-05-16 Compositions and methods for modulating mecp2 expression

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JP2015518712A true JP2015518712A (ja) 2015-07-06
JP2015518712A5 JP2015518712A5 (2) 2016-06-30

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US (3) US20150152410A1 (2)
EP (1) EP2850190B1 (2)
JP (1) JP2015518712A (2)
CN (1) CN104583402A (2)
AU (1) AU2013262709A1 (2)
CA (1) CA2873779A1 (2)
EA (1) EA201492116A1 (2)
WO (1) WO2013173608A1 (2)

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US12319913B2 (en) 2018-10-31 2025-06-03 The Research Foundation For The State University Of New York 5-halouracil-modified microRNAs and their use in the treatment of cancer

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